About Us

About Us

Our mission

Orphan Technologies is dedicated to helping patients control their homocysteine levels. We take the time to listen to what the patients and medical community are telling us. Through basic research and innovation we advance the field and bring new therapeutics to patients that improve patients’ lives.

Our Focus

Our lead program OT-58, is an enzyme therapy that addresses the underlying CBS deficit in patients living with homocystinuria and suffering from elevated homocysteine levels.